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utswmed.org
Closing in on a cure for Duchenne muscular dystrophy | Brain | Discovery | UT Southwestern Medical Center
Using an advanced gene editing technology called CRISPR, our team of scientists at UT Southwestern has been able to stop the progression of Duchenne muscular dystrophy in animals and human cells – a breakthrough that could ultimately change the prognosis for the most common fatal genetic disease in boys.
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