A regimen of three immune-suppressing drugs may improve the effectiveness of gene therapy for people with DMD, research in ...

Columnist Robin Stemple struggles to feel grateful on difficult days with FSHD, but still tries to recognize his many ...

New research shows DMD is marked by abnormalities in muscle development in the womb, supporting the potential of a therapy ...

Columnist Shalom Lim reflects with gratitude on how he's found purpose by supporting other Singaporeans on their own health ...

With three sons with Duchenne MD, columnist Betty Vertin has little time for housework, making her regret not giving the other kids chores.

Columnist Betty Vertin's track career ended years ago, but she never stopped lifting weights — only now its the emotional weight of Duchenne.

A Phase 1/2 clinical trial testing SRP-1003 for myotonic dystrophy type 1 is progressing with higher doses as planned.

The FDA updated prescribing information for Elevidys with new safety warnings and limiting its use to DMD patients who can ...

Agamree (vamorolone), a type of corticosteroid approved to help preserve muscle function in people with Duchenne muscular dystrophy (DMD), appears to work as well as traditional corticosteroids at ...