Guest writer Matthew Busch says that, despite the setbacks and surgeries he's endured, he's now thriving in life with Duchenne MD.

This verdict could spell the end for Translarna’s decades-long and tumultuous US DMD development journey.

Arriana Washington was arrested after the emaciated dog was discovered off Ingwood Avenue in New Smyrna Beach.

Azeem Ahmed launched Equal Clothing in 2023 to show those with severe disabilities that they can achieve their dreams - even if other people don't believe they can.

With the writing apparently on the wall, PTC Therapeutics has called off its latest bid for FDA approval of its Duchenne muscular dystrophy (DMD) drug Translarna.  | Late Thursday, PTC revealed that ...

PTC Therapeutics, Inc. (PTCT) stock closed lower following the withdrawal of its New Drug Application for Translarna by the FDA.

Regenxbio advances RGX-314 and RGX-202 pipelines for AMD and Duchenne while navigating recent FDA program setbacks. Read why RGNX stock is downgraded to buy.

After two decades of work with Translarna (ataluren) for nonsense mutation Duchenne muscular dystrophy, PTC Therapeutics Inc. withdrew its bid for approval of the compound upon hearing from the U.S.

PTC Therapeutics withdrew a New Drug Application for Translarna, a muscular dystrophy treatment, after the Food and Drug Administration indicated it would likely not grant approval.

PTC Therapeutics, Inc. (NASDAQ: PTCT) announced today that it has withdrawn the New Drug Application (NDA) resubmission for ...

Kim Ball felt like she was living in a dream when she learned she would be receiving a free, custom-built accessible van.

NMD Pharma A/S, a clinical-stage biotechnology company dedicated to developing novel therapies to restore skeletal muscle health, today announced that top-line data results from its Phase 2a ...