A 19-year-old Canadian man becomes the first human cured through prime gene editing after doctors corrected a rare genetic ...
A team of researchers at the Broad Institute, led by gene-editing pioneer David Liu, has developed a new genome-editing strategy that could potentially lead to a one-time treatment for multiple ...
The U.S. Food and Drug Administration approved the first cell-based gene therapies for sickle cell disease, including the ...
The firm believes that clinical data generated to date from two patients may be sufficient to support accelerated approval of PM359.