An Illinois family pushed for both boys to receive the potentially life changing medical treatment after one was approved and ...

An experimental gene therapy seems to slow the progression of Huntington’s disease by about 75 per cent, and researchers are ...

The first infant to undergo gene-editing therapy has accomplished another first — his first steps. KJ Muldoon is walking and ...

The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead of Christmas. KJ Muldoon is walking and getting ready to celebrate ...

Backed by a handful of prominent investors including the Gates Foundation, the startup is pursuing an approach it believes ...

Researchers hoped they had finally found a way to get gene therapies past the blood-brain barrier. Then the first patient ...

Zevaskyn, the first gene therapy for recessive dystrophic epidermolysis bullosa, showed significant wound healing in phase 3 trials.

JABSOM Cell and Molecular Biology researcher Dr. Jesse Owens has spent the better part of two decades chasing a vision that ...

Aradigm Health, a new benefits platform aimed at easing the financial sting of coverage for cell and gene therapies, has launched out of stealth. | Aradigm Health, new benefits platform aimed at ...

X-linked retinoschisis gene replacement therapy, aiming to improve retinal architecture and visual function in young male ...

There is no cure for the rare disease Hereditary Spastic Paraplegia (HSP), but researchers from Drexel University's College ...

The treatment uses a modified, harmless virus to deliver healthy genes to a patient’s cells to treat genetic diseases. Read ...